Infant receives world's first gene therapy for WOREE syndrome
Andreea Neblea
Hebrew University of Jerusalem Jun 8 2026 An eight-month-old infant with a severe genetic epilepsy has become the first patient in the world to receive an experimental gene replacement therapy designed to restore the function of the WWOX gene directly in the brain. The treatment, administered at Schneider Children's Medical Center of Israel, represents a significant milestone in the development of precision genetic therapies for rare neurological disorders. The therapy is based on more than a
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