New gene therapy is life changing for teenage patient
Orientul Mijlociu
A teenager with a rare, life-limiting genetic condition is off to university after receiving a pioneering gene therapy developed by researchers at UCL and Great Ormond Street Hospital for Children (GOSH). Remi, 19, received the treatment as part of a world-first trial at GOSH for the condition p47 Chronic Granulomatous Disease (CGD) which leaves patients vulnerable to severe infection and inflammation. The new gene therapy was developed by a team at UCL Great Ormond Street Institute of Child
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